Spinraza (nusinersen)

3 SMA type 1 patients show better finger, facial control with Spinraza

Three young people with severe spinal muscular atrophy (SMA) type 1 and treated with Spinraza (nusinersen) after their disease had already significantly advanced were seen by their caregivers to better control their finger and face movements, according to a Japanese report. The gains helped the patients, who depended…

Modified scoliosis surgery helps Spinraza treatment in severe cases

Modified surgery to correct a severe abnormal curvature of the spine in people with spinal muscular atrophy (SMA) allowed for reliable access to the spinal canal for Spinraza (nusinersen) injections, a small study shows. Spinraza, guided by ultrasound, was successfully administered through a small hole created in the…

Younger children on Spinraza made more motor function gains: Study

Being on Spinraza (nusinersen) for up to three years results in a gain in motor function for children with spinal muscular atrophy (SMA) type 2, with the youngest children benefiting the most from treatment, a small study has found. “It is therefore important to start the treatment as…