Author Archives: Diana Campelo Delgado

Grant Awarded to Find Affordable Treatments for Children

A researcher from Keele University School of Medicine in the U.K. was awarded a £99,959 ($138,633) research grant to identify and evaluate potential — and more affordable — treatments to improve the health of children with spinal muscular atrophy (SMA). The two-year research grant of the Academy of Medical…

TOPAZ Trial Results on Muscle Therapy Likely by June, Scholar Rock Says

Efficacy and safety results from the TOPAZ Phase 2 trial evaluating apitegromab, a  muscle-directed therapy for spinal muscular atrophy (SMA) being developed by Scholar Rock, are expected by June, the company announced. “2020 was a transformative year for Scholar Rock with … positive interim data from the…