Challenges of Life as Teen, Young Adult With SMA Highlighted in Survey

Challenges of Life as Teen, Young Adult With SMA Highlighted in Survey

Being an adolescent or young adult with spinal muscular atrophy (SMA) presents unique challenges, according to a study based on viewpoints expressed by patients ages 12 to 25. “‘I have SMA, SMA doesn’t have me’: a qualitative snapshot into the...

read more
CHMP Favors EU Approval of Evrysdi as 1st Oral, At-home SMA Treatment

CHMP Favors EU Approval of Evrysdi as 1st Oral, At-home SMA Treatment

Evrysdi (risdiplam) has been recommended for approval in the European Union (EU) to treat spinal muscular atrophy (SMA) patients, ages 2 months and older, with a clinical diagnosis of type 1, 2, or 3, or with one to four copies of the SMN2 “backup” gene. “Our close...

read more
Cure SMA Offers Free Virtual Therapy Sessions

Cure SMA Offers Free Virtual Therapy Sessions

To help with stress or anxiety brought on by the COVID-19 pandemic or other issues, adult patients with spinal muscular atrophy (SMA) in the U.S. are being offered up to three half-hour live video sessions with a licensed therapist. The Adults with SMA Virtual Therapy...

read more