Lake-Breaking SMA Treatment Insights You May Have Missed in February

Lake-Breaking SMA Treatment Insights You May Have Missed in February

February wrapped up with a surge of data on SMA, including novel investigations into how combinatorial therapies may provide new advantages to those with the disease. More information on how nusinersen impacts patients has also become available, as have new findings...
SMA HCP Roundup, mid-February: X-linked infantile SMA, Risdiplam News & More

SMA HCP Roundup, mid-February: X-linked infantile SMA, Risdiplam News & More

Research on SMA continues to forge ahead in 2020, with new results in from Roche’s latest investigation into its oral SMA drug, risdiplam. New tools for screening are being revealed as legislative changes are pushing more and more toward requiring infants born in the...
SMA HCP News November Round-up: Risdiplam, Early Treatment, NURTURE Study

SMA HCP News November Round-up: Risdiplam, Early Treatment, NURTURE Study

While the biggest news this week may be the success of the drug risdiplam in improving motor function in a late stage clinical trial on patients with SMA types 2 and 3,1 other important data on SMA have also been published in recent weeks. Below is a roundup of new...
SMA August Roundup: green kiwifruit extracts, abnormal fatty acid metabolism & updates on nusinersen and AVXS-101

SMA August Roundup: green kiwifruit extracts, abnormal fatty acid metabolism & updates on nusinersen and AVXS-101

Summer is closing with an abundance of new data on SMA. Studies aimed at understanding the disease process continue to provide information on its underlying mechanisms. At the same time, careful investigations of therapeutics are highlighting the potential of these...
Spinal Muscular Atrophy: Late-July Monthly Roundup

Spinal Muscular Atrophy: Late-July Monthly Roundup

In July, the literature pertaining to spinal muscular atrophy (SMA) has focused mainly on understanding the disease. Information on treatments has been published largely in review form, while there has also been some new information on managing the disease and what...