Respiratory Weakness in SMA Most Pronounced in Childhood, Study Finds
Lung function in people with earlier-onset forms of spinal muscular atrophy (SMA) tends to decline gradually throughout childhood and stabilizes in early adulthood, according to data from a population-based natural history study. The study, “Natural history of lung...
Lung Ultrasound Reliable Option to Chest X-rays for Monitoring Children
Lung ultrasound is a safe and reliable bedside tool to detect atelectasis (partial lung collapse) early in children with neuromuscular diseases, including spinal muscular atrophy (SMA), a study suggests. This radiation-free method could be used to monitor lung health...
FDA Approves AveXis’ Gene Therapy Zolgensma to Treat SMA in Children Up to Age 2
Zolgensma, a first gene therapy for spinal muscular atrophy — and first for any chronic neurologic disease — is now an approved and potential “one-time” intravenous treatment for pre-symptomatic newborns through 2-year-olds with any type of SMA, the U.S. Food and Drug...
What is Spinal Muscular Atrophy (SMA)?
Spinal Muscular Atrophy (SMA) is a congenital neuromuscular disorder characterized most prominently by progressive muscle atrophy and weakness.1 SMA is a neurodegenrative disease and the weakness and loss of muscle tone associated with SMA are the direct result...
Spinal Muscular Atrophy: Prognosis
The disease course and prognosis of spinal muscular atrophy (SMA) depends heavily on the clinical classification in a particular patient. For example, the prognosis of children with SMA type 0 is very poor while the prognosis in SMA type 4 patients is relatively good....HCP — SMA News Today
BioNews Services, LLC
3 W Garden St
Suite 354
Pensacola, FL 32502
Email: [email protected]
Phone: 1-800-936-1363